Dr. Darryl De Vivo explains how therapies have dramatically increased the lifespan of SMA patients
SMA Therapies
Good multidisciplinary care is recommended for people with SMA. This includes physical, occupational and respiratory therapies, as well as nutritional support. Increasing the amount of SMN protein produced by the body is now the main target of therapeutics development.
Current Therapies
People living with SMA often need continuous care from their families and from a variety of medical specialists for management of daily activities, nutrition, breathing, respiratory illnesses and to prepare for complications.
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Dr. De Vivo describes the current treatments and therapies for SMA -
Dr. De Vivo explains how therapies have dramatically increased the lifespan of SMA patients
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Esther and Frank describe the therapies in place for their 2 year old daughter, Maeve
Potential New Treatments
There are several promising new treatments for SMA aimed at increasing amount of SMN protein. However it takes many years for researchers to translate research from “bench to bedside."
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Dr. Sumner provides an overview of targets for SMA therapies -
Dr. Sumner describes small molecule therapies for SMA
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Dr. Sumner talks about gene therapy for SMA -
Dr. Sumner describes how early intervention is crucial when treating SMA
DNA Learning Center, © 2011 Cold Spring Harbor Laboratory. All Rights Reserved.
This project was supported by the SMA Foundation through the Cooperative Agreement Award 1H75DD000732-01 from the Centers for Disease Control and Prevention.